Rare and Orphan Diseases

Episodes 1-15 of 19

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  RestartResume

   Advancements in Understanding ALS Treatment

  Medical Industry Feature

   Advancements in Understanding ALS Treatment

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    Charles Turck, PharmD, BCPS, BCCCP

    Peer

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    Gustavo Suarez Zambrano, MD

    Peer

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  RestartResume

  Gene Therapy: Changing the Landscape of Hemophilia B Care

  Medical Industry Feature

  Gene Therapy: Changing the Landscape of Hemophilia B Care

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    Jennifer Caudle, DO

    Peer

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    Tammuella Chrisentery-Singleton, MD

    Peer

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  RestartResume

  From Symptoms to Diagnosis: Navigating ATTR Amyloidosis in Clinical Practice

  Medical Industry Feature

  From Symptoms to Diagnosis: Navigating ATTR Amyloidosis in Clinical Practice

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    Jennifer Caudle, DO

    Peer

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    Thomas Brannagan III, MD

    Peer

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    Marcus Anthony Urey, MD

    Peer

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  RestartResume

  Investigating a gMG Therapy, Part 1: The MG-ADL Results

  Medical Industry Feature

  Investigating a gMG Therapy, Part 1: The MG-ADL Results

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    Christyn Edmundson, MD

    Peer

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  RestartResume

  Investigating a gMG Therapy, Part 2: The Secondary Endpoint Results, Including MG Symptoms PRO

  Medical Industry Feature

  Investigating a gMG Therapy, Part 2: The Secondary Endpoint Results, Including MG Symptoms PRO

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    Christyn Edmundson, MD

    Peer

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  RestartResume

  Investigating a gMG Therapy, Part 3: Results from the Extension Studies

  Medical Industry Feature

  Investigating a gMG Therapy, Part 3: Results from the Extension Studies

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    Christyn Edmundson, MD

    Peer

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  RestartResume

  SCIg for Patient-Centric Care: Combining Experience with Innovation

  Medical Industry Feature

  SCIg for Patient-Centric Care: Combining Experience with Innovation

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    Matt Birnholz, MD

    Peer

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    Elena Perez, MD

    Peer

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  RestartResume

  Uncovering Unmet Needs in ATTR Amyloidosis

  Medical Industry Feature

  Uncovering Unmet Needs in ATTR Amyloidosis

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    Charles Turck, PharmD, BCPS, BCCCP

    Peer

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    Nitasha Sarswat, MD

    Peer

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  RestartResume

  Unraveling Hereditary ATTR Amyloidosis: Key Variants and Clinical Insights

  Medical Industry Feature

  Unraveling Hereditary ATTR Amyloidosis: Key Variants and Clinical Insights

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    Jennifer Caudle, DO

    Peer

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    Nitasha Sarswat, MD

    Peer

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    Thomas Brannagan III, MD

    Peer

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  RestartResume

  Clinical Insights into Higher-Risk MDS: Treatment Goals and Strategies

  Medical Industry Feature

  Clinical Insights into Higher-Risk MDS: Treatment Goals and Strategies

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    Gates B. Colbert, MD

    Peer

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    Uma Borate, MD

    Peer

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    James Dugan, MD

    Peer

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  RestartResume

  Improving Outcomes in hATTR-PN: The Role of Vigilant Symptom Assessment

  Medical Industry Feature

  Improving Outcomes in hATTR-PN: The Role of Vigilant Symptom Assessment

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    Jennifer Caudle, DO

    Peer

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    Thomas Brannagan III, MD

    Peer

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  RestartResume

  Expert Insights on Congenital Adrenal Hyperplasia Care From an Adult Endocrinologist

  Medical Industry Feature

  Expert Insights on Congenital Adrenal Hyperplasia Care From an Adult Endocrinologist

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    Sara Lubitz, MD

    Peer

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  RestartResume

  Expert Insights on Adult Congenital Adrenal Hyperplasia Care

  Medical Industry Feature

  Expert Insights on Adult Congenital Adrenal Hyperplasia Care

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    Sara Lubitz, MD

    Peer

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  RestartResume

  Breaking Down ATTR Pathophysiology

  Medical Industry Feature

  Breaking Down ATTR Pathophysiology

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    Marcus Anthony Urey, MD

    Peer

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  RestartResume

  Considerations for Time-limited Treatment in 1L Treatment Selection Decisions

  Medical Industry Feature

  Considerations for Time-limited Treatment in 1L Treatment Selection Decisions

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    Jennifer Caudle, DO

    Peer

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    Matthew Cortese, MD, MPH

    Peer

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