A genetic medicine at the heart of a $387 million Kyowa Kirin acquisition has won FDA approval, a regulatory decision that makes the one-time treatment the first approved therapy for the rare inherited disorder metachromatic leukodystrophy (MLD). In the most severe form of MLD, babies develop nor…
Credit: Pixabay/CC0 Public Domain Researchers from Children's Hospital of Philadelphia (CHOP) identified a key metabolite in cells that helps direct immune responses and explains at a single cell leve…
Using single-cell sequencing technology, researchers provide the most comprehensive timeline to date of how the body responds to SARS-CoV-2 exposure. Email newsletter News and blog updates Sign up …
In testing, Wenzel's "mini-brains" more accurately reflect a fully-fledged adult human brain, so they can be used to more closely examine neurological conditions of adult patients, such as Alzheimer disease. And for those “mini-brains” created from the stem cells of individuals who have Alzheimer’s…
Research shows chemicals in countless household items harm specialized cells in the brain A team of researchers from Case Western Reserve University School of Medicine has provided fresh insight into the dangers some common household chemicals pose to brain health. Th…
Deletion of A2B receptors in hippocampal astrocytes. Credit: Nature (2024). DOI: 10.1038/s41586-024-07611-w A key mechanism which detects when the brain needs an additional energy boost to support its…
Using spatial analysis of tissue samples, Cedars-Sinai investigators have identified patterns that could predict whether patients with the most common type of ovarian cancer will experience early relapse after treatment. These patterns, detailed in a study published in the peer…
We're another step closer to reducing the need for round-the-clock insulin injections to manage diabetes after a new study showed how insulin-producing cells could be regenerated in the pancreas.The breakthrough was made by getting pancreatic ductal progenitor cells – that give rise to the tissues…
CCOC and ENOC resemble different phases of normal cyclic endometrium based on gene expression profile. Credit: Cancer Research (2023). DOI: 10.1158/0008-5472.CAN-23-1362 Two types of endometriosis-rel…