Host Dr. Bruce Bloom welcomes Dr. Emil Kakkis, an advisor at BioMarin Pharmaceutical Inc. and author of numerous published articles on mucopolysaccharidosis I, or MPS I, to discuss current treatment options. They discuss the benefits and risks of enzyme replacement therapy with laronidase.
Don't miss these other programs on MPS I, with host Dr. Bruce Bloom:
Challenges in Management of MPS I
Immune System Irregularities in Lysosomal Storage Disorders
Musculoskeletal Aspects of MPS I: Diagnosis and Management Considerations